Search results for "Corneal clouding"

showing 3 items of 3 documents

Clinical heterogeneity in infantile galactosialidosis

1987

A new case of infantile galactosialidosis is presented. The condition was diagnosed when the patient was 4 months of age and she died at 20 months. She exhibited some of the symptoms of classical infantile galactosialidosis but no corneal clouding, cherry-red macular spot or limitation of joint mobility. Sonographic examination showed large kidneys and thickened cardiac septa, two symptoms as yet undescribed in this disorder. Urinary oligosaccharide analysis gave grossly pathological results and subsequent fibroblast enzyme analysis showed a deficiency of alpha-neuraminidase and beta-galactosidase. The patient's clinical features are compared with the few cases so far described in the liter…

Pathologymedicine.medical_specialtyUrinary systemNeuraminidaseOligosaccharidesLarge kidneysKidneyLactose IntoleranceJoint mobilityCorneal cloudingClinical heterogeneityHumansMedicinePathologicalUltrasonographybusiness.industryMyocardiumInfantFibroblastsbeta-Galactosidasemedicine.diseaseGalactosidasesPediatrics Perinatology and Child HealthFemalebusinessGalactosialidosisEuropean Journal of Pediatrics
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Ophthalmological Findings in Mucopolysaccharidoses

2019

The mucopolysaccharidoses (MPS) are a heterogenous group of lysosomal storage disorders caused by the accumulation of glycosaminoglycans (GAGs). The accrual of these compounds results in phenotypically varied syndromes that produce multi-organ impairment with widespread systemic effects. The low incidence of MPS (approximately 1/25,000 live births) in conjunction with the high childhood mortality rate had limited the availability of research into certain clinical features, especially ocular manifestations. As the recent successes of hematopoietic stem cell transplantation (HSCT) and enzyme replacement therapy (ERT) have greatly increased life expectancy in these patients, they have served a…

0301 basic medicinecongenital hereditary and neonatal diseases and abnormalitiesPediatricsmedicine.medical_specialtygenetic structuresmedicine.medical_treatmentMucopolysaccharidosislcsh:MedicineGlaucomaReviewHematopoietic stem cell transplantation03 medical and health sciences0302 clinical medicineQuality of lifeCorneal cloudingmedicinebusiness.industryMortality rateIncidence (epidemiology)lcsh:Rnutritional and metabolic diseasesmucopolysaccharidosisGeneral MedicineEnzyme replacement therapymedicine.diseaseocular manifestationseye diseasesophthalmology030104 developmental biologycorneal clouding030221 ophthalmology & optometrylysosomal storage disordersense organsbusinessJournal of Clinical Medicine
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Measuring corneal clouding in patients suffering from mucopolysaccharidosis with the Pentacam densitometry programme

2013

Aim To identify a means to objectively measure corneal clouding in patients with mucopolysaccharidosis in a prospective controlled clinical trial. Methods Corneal haze was assessed by slit lamp examination and measured using the densitometry programme of the Pentacam, a rotating Scheimpflug camera in 33 mucopolysaccharidoses (MPS) patients and 32 controls. Results Pentacam measurements were available in 31 right and 31 left eyes of 32 patients and in 32 left and right eyes of 32 subjects in the control group. Slit lamp findings correlated very well with corneal density measurements (Spearman correlation right eye (OD)/left eye (OS)=0.782/0.791). MPS patients had higher density units (median…

AdultMalemedicine.medical_specialtyAdolescentgenetic structuresMucopolysaccharidosisScheimpflug principleVisual AcuityDiagnostic Techniques OphthalmologicalYoung AdultCellular and Molecular NeuroscienceCorneal OpacityCorneaCorneal cloudingOphthalmologyPhotographymedicineHumansIn patientProspective StudiesChildSlit lampCorneal Hazebusiness.industryMiddle AgedMucopolysaccharidosesmedicine.diseaseeye diseasesSensory SystemsSurgeryOphthalmologymedicine.anatomical_structureChild PreschoolFemalesense organsbusinessDensitometryDensitometryBritish Journal of Ophthalmology
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